Ignite Creation Date:
2025-12-24 @ 9:54 PM
Ignite Modification Date:
2026-05-17 @ 1:58 PM
Study NCT ID:
NCT04877132
Status:
APPROVED_FOR_MARKETING
Last Update Posted:
2022-09-19
First Post:
2021-05-03
Is NOT Gene Therapy:
True
Has Adverse Events:
False
Brief Title:
Compassionate Use Program for Olipudase Alfa Enzyme Replacement Therapy for Patients With Chronic Acid Sphingomyelinase Deficiency (ASMD)
Sponsor:
Organization: