Viewing Study NCT04480567


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Ignite Modification Date: 2026-01-25 @ 3:29 AM
Study NCT ID: NCT04480567
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2024-12-12
First Post: 2020-07-08
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: AAV Gene Therapy Study for Subjects with PKU
Sponsor: BioMarin Pharmaceutical
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: 307-201
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators