Viewing Study NCT04480567

Home Icon Home Search Icon Search Certify Doc Icon Certify Doc Certify Doc Icon Genes Certify Doc Icon Clinical Trials Certify Doc Icon CompTox Processes Icon DrugMatrix Open Targets Icon Open Targets Processes Icon Products Support Icon Support Bugs Icon Bugs
Main Search Make This Study a Gene Therapy Make This Study a Not Gene Therapy Report Bug
Ignite Creation Date: 2025-12-25 @ 12:29 AM
Ignite Modification Date: 2026-07-01 @ 6:52 AM
Study NCT ID: NCT04480567
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2024-12-12
First Post: 2020-07-08
Is NOT Gene Therapy: True
Has Adverse Events: False
Brief Title: AAV Gene Therapy Study for Subjects with PKU
Sponsor: BioMarin Pharmaceutical
Organization:
Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Phenylketonuria (PKU) View
Keywords:

Keywords

Keyword Brief Keyword Text View
None PKU View
None PAH Deficiency View