Viewing Study NCT01362595


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Study NCT ID: NCT01362595
Status: COMPLETED
Last Update Posted: 2022-12-02
First Post: 2011-05-20
Is Gene Therapy: True
Has Adverse Events: True

Brief Title: Pilot Phase I/II Study of Amino Acid Leucine in Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia
Sponsor: Northwell Health
Organization:

Organization Data

Organization:
Class: OTHER
Study ID: 12-375B
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: OTHER
Responsible Party:
Responsible Party Title:
Responsible Party Type: PRINCIPAL_INVESTIGATOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators