Viewing Study NCT04729751


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Study NCT ID: NCT04729751
Status: COMPLETED
Last Update Posted: 2025-02-06
First Post: 2021-01-25
Is NOT Gene Therapy: False
Has Adverse Events: False

Brief Title: A Study to Evaluate the Safety and Tolerability of Maralixibat in Infant Participants With Cholestatic Liver Diseases Including Progressive Familial Intrahepatic Cholestasis (PFIC) and Alagille Syndrome (ALGS).
Sponsor: Mirum Pharmaceuticals, Inc.
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: MRX-801
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators