Viewing Study NCT04729751


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Study NCT ID: NCT04729751
Status: COMPLETED
Last Update Posted: 2025-02-06
First Post: 2021-01-25
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: A Study to Evaluate the Safety and Tolerability of Maralixibat in Infant Participants With Cholestatic Liver Diseases Including Progressive Familial Intrahepatic Cholestasis (PFIC) and Alagille Syndrome (ALGS).
Sponsor: Mirum Pharmaceuticals, Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Progressive Familial Intrahepatic Cholestasis View
None Alagille Syndrome View
None Cholestatic Liver Disease View
Keywords:

Keywords

Keyword Brief Keyword Text View
None PFIC View
None ALGS View
None Maralixibat View
None Bile Duct Diseases View
None Liver Diseases View
None Biliary Tract Diseases View
None Pediatric View