Viewing Study NCT05906251


Ignite Creation Date: 2025-12-24 @ 11:46 PM
Ignite Modification Date: 2026-05-20 @ 5:18 AM
Study NCT ID: NCT05906251
Status: TERMINATED
Last Update Posted: 2025-09-04
First Post: 2023-06-07
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: A Gene Transfer Study to Evaluate the Safety, Tolerability and Efficacy of SRP-6004 in Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2B/R2 (LGMD2B/R2, Dysferlin [DYSF] Related)
Sponsor: Sarepta Therapeutics, Inc.
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: SRP-6004-102
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators