Viewing Study NCT05634512


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Ignite Modification Date: 2026-03-04 @ 7:50 PM
Study NCT ID: NCT05634512
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-10-30
First Post: 2022-11-22
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Evaluation of Intravenous Laronidase Pharmacokinetics Before and After Hematopoietic Cell Transplantation in Patients With Mucopolysaccharidosis Type IH.
Sponsor: Masonic Cancer Center, University of Minnesota
Organization:

Organization Data

Organization:
Class: OTHER
Study ID: 2021LS144
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: OTHER
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators