Viewing Study NCT06092034


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Ignite Modification Date: 2025-12-28 @ 12:15 AM
Study NCT ID: NCT06092034
Status: RECRUITING
Last Update Posted: 2025-10-07
First Post: 2023-10-11
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease
Sponsor: Rocket Pharmaceuticals Inc.
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: RP-A501-0123
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators