Viewing Study NCT06092034


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Ignite Modification Date: 2026-06-06 @ 7:34 PM
Study NCT ID: NCT06092034
Status: RECRUITING
Last Update Posted: 2025-10-07
First Post: 2023-10-11
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease
Sponsor: Rocket Pharmaceuticals Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Danon Disease View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Hypertrophic Cardiomyopathy View
None HCM View
None X-linked disease View
None LAMP2 View
None Pediatric View
None Skeletal Myopathies View
None Cardiomyopathy View
None Lysosomal Storage Disorder View
None Left Ventricular Hypertrophy View