Viewing Study NCT05444894


Ignite Creation Date: 2025-12-25 @ 1:46 AM
Ignite Modification Date: 2026-06-04 @ 4:28 AM
Study NCT ID: NCT05444894
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-04-02
First Post: 2022-06-27
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: EDIT-301 for Autologous Hematopoietic Stem Cell Transplant (HSCT) in Participants With Transfusion-Dependent Beta Thalassemia (TDT)
Sponsor: Editas Medicine, Inc.
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: EM-301-BThal-001
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators