Viewing Study NCT06971094


Ignite Creation Date: 2025-12-25 @ 1:27 AM
Ignite Modification Date: 2026-05-06 @ 10:53 AM
Study NCT ID: NCT06971094
Status: RECRUITING
Last Update Posted: 2025-06-05
First Post: 2025-05-06
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Safety and Efficacy Evaluation of GC101 Gene Therapy Via Intrathecal (IT) Injectionin the Treatment of Patients With Type 2 Spinal Muscular Atrophy (SMA) - Phase III
Sponsor: GeneCradle Inc
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: JLJY-GC101-SMA-011
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators