Viewing Study NCT03612869


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Ignite Modification Date: 2026-05-29 @ 11:55 AM
Study NCT ID: NCT03612869
Status: UNKNOWN
Last Update Posted: 2021-08-31
First Post: 2018-07-04
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Study of AAVrh10-h.SGSH Gene Therapy in Patients With Mucopolysaccharidosis Type IIIA (MPS IIIA)
Sponsor: LYSOGENE
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module