Viewing Study NCT01747135


Ignite Creation Date: 2025-12-24 @ 10:37 PM
Ignite Modification Date: 2026-07-12 @ 4:16 PM
Study NCT ID: NCT01747135
Status: COMPLETED
Last Update Posted: 2021-07-23
First Post: 2012-12-08
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Hydroxypropyl Beta Cyclodextrin for Niemann-Pick Type C1 Disease
Sponsor:
Organization: