Viewing Study NCT01016392


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Ignite Modification Date: 2026-04-18 @ 4:46 PM
Study NCT ID: NCT01016392
Status: COMPLETED
Last Update Posted: 2022-04-15
First Post: 2009-11-18
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Observational Study on the Long Term Safety of KuvanĀ® Treatment in Patients With Hyperphenylalaninemia (HPA) Due to Phenylketonuria (PKU) or BH4 Deficiency
Sponsor:
Organization: