Viewing Study NCT04480567


Ignite Creation Date: 2025-12-25 @ 12:29 AM
Ignite Modification Date: 2025-12-31 @ 11:12 PM
Study NCT ID: NCT04480567
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2024-12-12
First Post: 2020-07-08
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: AAV Gene Therapy Study for Subjects with PKU
Sponsor: BioMarin Pharmaceutical
Organization:

Key Dates - Follows AllAPIJSON File Order

Start Date: 2020-09-24
Start Date Type: ACTUAL
Primary Completion Date: 2027-12
Primary Completion Date Type: ESTIMATED
Completion Date: 2027-12
Completion Date Type: ESTIMATED
First Submit Date: 2020-07-08
First Submit QC Date: None
Study First Post Date: 2020-07-21
Study First Post Date Type: ACTUAL
Results First Submit Date: None
Results First Submit QC Date: None
Results First Post Date: None
Results First Post Date Type: None
Results First Post QC Date: None
Results First Post QC Date Type: None
Disp First Submit Date: None
Disp First Submit QC Date: None
Disp First Post Date: None
Disp First Post Date Type: None
Last Update Submit Date: 2024-12-09
Last Update Post Date: 2024-12-12
Last Update Post Date Type: ACTUAL