Viewing Study NCT01362595


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Study NCT ID: NCT01362595
Status: COMPLETED
Last Update Posted: 2022-12-02
First Post: 2011-05-20
Is NOT Gene Therapy: True
Has Adverse Events: True

Brief Title: Pilot Phase I/II Study of Amino Acid Leucine in Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia
Sponsor: Northwell Health
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Diamond Blackfan Anemia View
None Blackfan Diamond Syndrome View
None DBA View
None Congenital Hypoplastic Anemia View
None Pure Red Cell Aplasia View
Keywords:

Keywords

Keyword Brief Keyword Text View
None leucine administration View
None red blood cell transfusion View
None Diamond Blackfan anemia View