Viewing Study NCT04755751


Ignite Creation Date: 2025-12-24 @ 11:47 PM
Ignite Modification Date: 2026-07-10 @ 3:18 AM
Study NCT ID: NCT04755751
Status: UNKNOWN
Last Update Posted: 2021-02-16
First Post: 2021-02-10
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Exercise Capacity in Response to Enzyme Replacement Therapy in Pediatric Pompe Disease.
Sponsor: Rambam Health Care Campus
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Pompe Disease Infantile-Onset View
Keywords: