Viewing Study NCT02097251

Home Icon Home Search Icon Search Certify Doc Icon Certify Doc Certify Doc Icon Genes Certify Doc Icon Clinical Trials Certify Doc Icon CompTox Processes Icon DrugMatrix Open Targets Icon Open Targets Processes Icon Products Support Icon Support Bugs Icon Bugs
Main Search Make This Study a Gene Therapy Make This Study a Not Gene Therapy Report Bug
Ignite Creation Date: 2025-12-24 @ 11:40 PM
Ignite Modification Date: 2026-05-29 @ 9:31 PM
Study NCT ID: NCT02097251
Status: NO_LONGER_AVAILABLE
Last Update Posted: 2017-02-06
First Post: 2014-03-24
Is Gene Therapy: True
Has Adverse Events: False
Brief Title: An Open-Label Treatment Protocol With UX003 rhGUS Enzyme Replacement Therapy for an Advanced Stage MPS 7 Patient
Sponsor: Joyce Fox
Organization:
Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Mucopolysaccharidosis Type 7 View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Mucopolysaccharidosis Type 7 View
None Sly syndrome View
None UX003 View
None Enzyme Replacement Therapy View
None rare disease View
None Lysosomal Storage Disease View
None metabolic disorder View