Viewing Study NCT01747135


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Study NCT ID: NCT01747135
Status: COMPLETED
Last Update Posted: 2021-07-23
First Post: 2012-12-08
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Hydroxypropyl Beta Cyclodextrin for Niemann-Pick Type C1 Disease
Sponsor: Vtesse, LLC, a Mallinckrodt Pharmaceuticals Company
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Niemann-Pick Disease, Type C1 View
Keywords:

Keywords

Keyword Brief Keyword Text View
None 2-Hydroxypropyl-B-Cyclodextrin View
None Niemann-Pick Disease, Type C1 View
None Neurodegeneration View