Viewing Study NCT00051935

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Ignite Creation Date: 2025-12-24 @ 10:35 PM
Ignite Modification Date: 2026-07-07 @ 9:46 AM
Study NCT ID: NCT00051935
Status: COMPLETED
Last Update Posted: 2014-02-05
First Post: 2003-01-17
Is Gene Therapy: True
Has Adverse Events: False
Brief Title: A Study of the Safety and Pharmacokinetics of rhGAA in Siblings With Glycogen Storage Disease Type II
Sponsor: Genzyme, a Sanofi Company
Organization:
Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Glycogen Storage Disease Type II View
None Pompe Disease View
None Acid Maltase Deficiency Disease View
None Glycogenosis 2 View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Glycogen Storage Disease Type II View
None GSD-II View
None Pompe Disease View