Viewing Study NCT04877132


Ignite Creation Date: 2025-12-24 @ 9:54 PM
Ignite Modification Date: 2026-01-02 @ 12:44 AM
Study NCT ID: NCT04877132
Status: APPROVED_FOR_MARKETING
Last Update Posted: 2022-09-19
First Post: 2021-05-03
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Compassionate Use Program for Olipudase Alfa Enzyme Replacement Therapy for Patients With Chronic Acid Sphingomyelinase Deficiency (ASMD)
Sponsor: Sanofi
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Sphingomyelin Lipidosis View
Keywords: