Viewing Study NCT00919503


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Study NCT ID: NCT00919503
Status: COMPLETED
Last Update Posted: 2021-08-13
First Post: 2009-06-11
Is NOT Gene Therapy: True
Has Adverse Events: True

Brief Title: Treosulfan and Fludarabine Phosphate Before Donor Stem Cell Transplant in Treating Patients With Nonmalignant Inherited Disorders
Sponsor: Fred Hutchinson Cancer Center
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Non-Neoplastic Hematologic and Lymphocytic Disorder View
Keywords:

Keywords

Keyword Brief Keyword Text View
None nonmalignant diseases View
None nonmalignant inherited disorders View
None primary immunodeficiency diseases View
None primary immune deficiency disorders View
None chronic granulomatous View
None disease View
None IPEX syndrome View
None hemophagocytic lymphohistiocytosis View
None Wiskott Aldrich Syndrome View
None bone marrow failure syndromes View
None Shwachman Diamond Syndrome View
None Dyskeratosis Congenita View
None Diamond Blackfan Anemia View
None inborn errors of metabolism View
None metabolic diseases View
None hemoglobinopathies View
None sickle cell disease View
None thalassemia View
None reduced intensity transplantation View
None hematopoietic cell transplantation View
None bone marrow transplantation View
None umbilical cord blood transplantation View