Viewing Study NCT01840657


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Ignite Modification Date: 2026-05-23 @ 10:05 AM
Study NCT ID: NCT01840657
Status: COMPLETED
Last Update Posted: 2018-03-07
First Post: 2013-04-18
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Myotubular Myopathy Event Study
Sponsor: Cure CMD
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None X-linked Myotubular Myopathy View
Keywords:

Keywords

Keyword Brief Keyword Text View
None CMDIR (Congenital Muscle Disease International Registry) View
None X-linked myotubular myopathy View
None centronuclear myopathy View
None myotubularin View
None MTM1 gene View
None mutation View
None survival View
None adverse event View
None disease complication View
None hospital admission View
None emergency room visit View
None motor function View
None respiratory function View
None natural history study View