Viewing Study NCT04702568


Ignite Creation Date: 2025-12-24 @ 6:29 PM
Ignite Modification Date: 2026-05-07 @ 3:37 AM
Study NCT ID: NCT04702568
Status: TERMINATED
Last Update Posted: 2025-04-13
First Post: 2021-01-07
Is NOT Gene Therapy: True
Has Adverse Events: True

Brief Title: A Long-Term Safety Study of BCX9930 in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH)
Sponsor: BioCryst Pharmaceuticals
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Paroxysmal Nocturnal Hemoglobinuria View
None PNH View
Keywords:

Keywords

Keyword Brief Keyword Text View
None BCX9930 View
None Factor D inhibitor View
None PNH View
None paroxysmal Nocturnal Hemoglobinuria View
None oral treatment View