Viewing Study NCT01721733

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Ignite Creation Date: 2025-12-25 @ 2:41 AM
Ignite Modification Date: 2026-04-14 @ 10:40 PM
Study NCT ID: NCT01721733
Status: COMPLETED
Last Update Posted: 2020-08-31
First Post: 2012-11-01
Is NOT Gene Therapy: True
Has Adverse Events: False
Brief Title: Safety and Efficacy Study of EPI-743 in Children With Leigh Syndrome
Sponsor: PTC Therapeutics
Organization:
Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Leigh Syndrome View
Keywords:

Keywords

Keyword Brief Keyword Text View
None EPI743 View
None Leigh syndrome View
None respiratory chain disease View
None mitochondrial disorders View