Viewing Study NCT04797260


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Study NCT ID: NCT04797260
Status: RECRUITING
Last Update Posted: 2024-04-18
First Post: 2021-03-11
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Phase I/II Clinical Trial Stem Cell Gene Therapy in RAG1-Deficient SCID
Sponsor: Leiden University Medical Center
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Severe Combined Immunodeficiency Due to RAG1 Deficiency View
Keywords:

Keywords

Keyword Brief Keyword Text View
None SCID View
None RAG1 View
None Gene Therapy View