Viewing Study NCT05444894


Ignite Creation Date: 2025-12-25 @ 1:46 AM
Ignite Modification Date: 2025-12-31 @ 2:34 PM
Study NCT ID: NCT05444894
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-04-02
First Post: 2022-06-27
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: EDIT-301 for Autologous Hematopoietic Stem Cell Transplant (HSCT) in Participants With Transfusion-Dependent Beta Thalassemia (TDT)
Sponsor: Editas Medicine, Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Transfusion Dependent Beta Thalassemia View
None Hemoglobinopathies View
None Thalassemia Major View
None Thalassemia Intermedia View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Beta-Thalassemia View
None Hemoglobinopathies View
None CRISPR-Cas 12a View
None Autologous CD34+ View