Viewing Study NCT04530994


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Study NCT ID: NCT04530994
Status: APPROVED_FOR_MARKETING
Last Update Posted: 2021-10-20
First Post: 2020-08-25
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: A Maralixibat Expanded Access Program for Patients With Cholestatic Pruritus Associated With Alagille Syndrome (ALGS)
Sponsor: Mirum Pharmaceuticals, Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Alagille Syndrome View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Liver Disease View
None ALGS View
None Maralixibat View
None Bile Duct Diseases View
None Digestive System Diseases View
None Biliary Tract Diseases View
None Cholestasis View
None Pruritis View