Viewing Study NCT05523206


Ignite Creation Date: 2025-12-26 @ 5:20 PM
Ignite Modification Date: 2026-02-06 @ 6:12 AM
Study NCT ID: NCT05523206
Status: COMPLETED
Last Update Posted: 2025-01-30
First Post: 2022-08-29
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: A Natural History Study of Biomarkers and Clinical Outcomes in Mucopolysaccharidosis Type IIIA (MPS IIIA; Sanfilippo Syndrome)
Sponsor:
Organization: