Ignite Creation Date:
2025-12-24 @ 11:36 PM
Ignite Modification Date:
2026-01-31 @ 9:24 PM
Study NCT ID:
NCT05089656
Status:
COMPLETED
Last Update Posted:
2025-12-08
First Post:
2021-10-11
Is Gene Therapy:
True
Has Adverse Events:
True
Brief Title:
Efficacy and Safety of Intrathecal OAV101 (AVXS-101) in Pediatric Patients With Type 2 Spinal Muscular Atrophy (SMA)
Sponsor:
Organization: