Viewing Study NCT05236595


Ignite Creation Date: 2025-12-24 @ 1:39 PM
Ignite Modification Date: 2026-01-26 @ 7:56 PM
Study NCT ID: NCT05236595
Status: ENROLLING_BY_INVITATION
Last Update Posted: 2025-02-21
First Post: 2021-12-27
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Research for Individualized Therapeutics in Rare Genetic Disease
Sponsor:
Organization: