Viewing Study NCT04041102


Ignite Creation Date: 2025-12-25 @ 3:39 AM
Ignite Modification Date: 2026-01-25 @ 5:47 AM
Study NCT ID: NCT04041102
Status: COMPLETED
Last Update Posted: 2025-10-24
First Post: 2019-07-16
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Natural History Study of Infantile and Juvenile GM1 Gangliosidosis (GM1) Patients
Sponsor:
Organization: