Viewing Study NCT04120493


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Ignite Modification Date: 2026-02-25 @ 5:51 PM
Study NCT ID: NCT04120493
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-10-21
First Post: 2019-09-30
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Safety and Proof-of-Concept (POC) Study With AMT-130 in Adults With Early Manifest Huntington's Disease
Sponsor: UniQure Biopharma B.V.
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: CT-AMT-130-01
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators