Viewing Study NCT04601051


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Ignite Modification Date: 2025-12-25 @ 9:51 PM
Study NCT ID: NCT04601051
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-05-01
First Post: 2020-10-19
Is NOT Gene Therapy: False
Has Adverse Events: False

Brief Title: Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of NTLA-2001 in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy (ATTRv-PN) and Patients With Transthyretin Amyloidosis-Related Cardiomyopathy (ATTR-CM)
Sponsor: Intellia Therapeutics
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: ITL-2001-CL-001
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators