Viewing Study NCT06283212


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Ignite Modification Date: 2025-12-30 @ 11:05 PM
Study NCT ID: NCT06283212
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-12-12
First Post: 2024-02-22
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Children With SCN1A-positive Dravet Syndrome
Sponsor: Encoded Therapeutics
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: ETX-DS-005
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators