Ignite Creation Date:
2025-12-24 @ 10:41 PM
Ignite Modification Date:
2026-01-02 @ 10:40 AM
Study NCT ID:
NCT04669535
Status:
TERMINATED
Last Update Posted:
2025-09-02
First Post:
2020-11-23
Is NOT Gene Therapy:
True
Has Adverse Events:
True
Brief Title:
A Dose-escalation and Safety & Efficacy Study of AXO-AAV-GM2 in Tay-Sachs or Sandhoff Disease
Sponsor:
Terence Flotte
Organization:
Organization Data
Organization:
Class:
OTHER
Study ID:
AXO-GM2-001
Study Type:
None
Study Domain:
None
Study Link:
None
Lead Sponsor:
Lead Sponsor Class:
OTHER
Responsible Party:
Responsible Party Title:
Responsible Party Type:
SPONSOR_INVESTIGATOR
Responsible Party Affiliation:
Old Name:
None
Old Organization:
None