Viewing Study NCT05356195


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Ignite Modification Date: 2025-12-30 @ 3:37 PM
Study NCT ID: NCT05356195
Status: RECRUITING
Last Update Posted: 2025-10-14
First Post: 2022-04-07
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT)
Sponsor: Vertex Pharmaceuticals Incorporated
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: VX21-CTX001-141
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators

Collaborators

Name Class View
None INDUSTRY View