Viewing StudyNCT06369974



Ignite Creation Date: 2024-05-06 @ 8:23 PM
Last Modification Date: 2024-10-26 @ 3:27 PM
Study NCT ID: NCT06369974
Status: NOT_YET_RECRUITING
Last Update Posted: 2024-04-18
First Post: 2024-03-11

Brief Title: Single Participant Study of an Experimental ASO Treatment for TUBB4A-related Leukodystrophy
Sponsor: Massachusetts General Hospital
Organization: Massachusetts General Hospital

Organization Data

Organization: Massachusetts General Hospital
Class: OTHER
Study ID: 2024P000386
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor: Massachusetts General Hospital
Lead Sponsor Class: OTHER
Responsible Party: Florian Eichler
Responsible Party Title: Director of the Center for Rare Neurological Diseases
Responsible Party Type: PRINCIPAL_INVESTIGATOR
Responsible Party Affiliation: Massachusetts General Hospital
Old Name: None
Old Organization: None

Collaborators

Name Class
n-Lorem Foundation OTHER