Viewing StudyNCT06314490



Ignite Creation Date: 2024-05-06 @ 8:15 PM
Last Modification Date: 2024-10-26 @ 3:24 PM
Study NCT ID: NCT06314490
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2024-03-18
First Post: 2024-03-01

Brief Title: Personalized Antisense Oligonucleotide Therapy for Rare Pediatric Genetic Disease SCN2A
Sponsor: University of California San Diego
Organization: University of California San Diego

Organization Data

Organization: University of California San Diego
Class: OTHER
Study ID: ASOSCN2A
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor: University of California San Diego
Lead Sponsor Class: OTHER
Responsible Party: Olivia Kim-McManus
Responsible Party Title: Professor Neurosciences
Responsible Party Type: PRINCIPAL_INVESTIGATOR
Responsible Party Affiliation: University of California San Diego
Old Name: None
Old Organization: None

Collaborators

Name Class
California Institute for Regenerative Medicine CIRM OTHER
n-Lorem Foundation OTHER