Viewing StudyNCT05876780



Ignite Creation Date: 2024-05-06 @ 7:02 PM
Last Modification Date: 2024-10-26 @ 2:59 PM
Study NCT ID: NCT05876780
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2023-09-21
First Post: 2023-05-17

Brief Title: A Gene Transfer Single Dose Study to Evaluate the Safety Tolerability and Efficacy of SRP-9003 in Non-Ambulatory and Ambulatory Participants With Limb Girdle Muscular Dystrophy Type 2ER4 Beta-Sarcoglycan β-SG Deficiency
Sponsor: Sarepta Therapeutics Inc
Organization: Sarepta Therapeutics Inc

Organization Data

Organization: Sarepta Therapeutics Inc
Class: INDUSTRY
Study ID: SRP-9003-102
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor: Sarepta Therapeutics Inc
Lead Sponsor Class: INDUSTRY
Responsible Party: None
Responsible Party Title: None
Responsible Party Type: SPONSOR
Responsible Party Affiliation: None
Old Name: None
Old Organization: None

Collaborators