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Ignite Creation Date:
2024-05-06 @ 6:26 PM
Last Modification Date:
2024-10-26 @ 2:48 PM
Study NCT ID:
NCT05665166
Status:
RECRUITING
Last Update Posted:
2023-10-12
First Post:
2022-12-07
Brief Title:
Gene Therapy with Modified Autologous Hematopoietic Stem Cells for Patients with Mucopolysaccharidosis Type II
Sponsor:
University of Manchester
Organization:
University of Manchester
Overview
Dates
Organization
Conditions
Design
Enrollment
Locations
Outcomes
Organization Data
Organization:
University of Manchester
Class:
OTHER
Study ID:
R125432
Study Type:
None
Study Domain:
None
Study Link:
None
Lead Sponsor:
University of Manchester
Lead Sponsor Class:
OTHER
Responsible Party:
None
Responsible Party Title:
None
Responsible Party Type:
SPONSOR
Responsible Party Affiliation:
None
Old Name:
None
Old Organization:
None
Collaborators
Name
Class
Manchester University NHS Foundation Trust
OTHER_GOV
AVROBIO
INDUSTRY
CTI Clinical Trial and Consulting Services
OTHER
Great Ormond Street Hospital for Children NHS Foundation Trust
OTHER