Viewing StudyNCT05477563



Ignite Creation Date: 2024-05-06 @ 5:54 PM
Last Modification Date: 2024-10-26 @ 2:38 PM
Study NCT ID: NCT05477563
Status: RECRUITING
Last Update Posted: 2024-05-16
First Post: 2022-07-26

Brief Title: Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease
Sponsor: Vertex Pharmaceuticals Incorporated
Organization: Vertex Pharmaceuticals Incorporated

Organization Data

Organization: Vertex Pharmaceuticals Incorporated
Class: INDUSTRY
Study ID: VX21-CTX001-161
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor: Vertex Pharmaceuticals Incorporated
Lead Sponsor Class: INDUSTRY
Responsible Party: None
Responsible Party Title: None
Responsible Party Type: SPONSOR
Responsible Party Affiliation: None
Old Name: None
Old Organization: None

Collaborators

Name Class
CRISPR Therapeutics INDUSTRY