Viewing StudyNCT04855045



Ignite Creation Date: 2024-05-06 @ 4:04 PM
Last Modification Date: 2024-10-26 @ 2:02 PM
Study NCT ID: NCT04855045
Status: UNKNOWN
Last Update Posted: 2022-03-25
First Post: 2021-04-13

Brief Title: An Open-label Dose Escalation and Double-masked Randomized Controlled Trial Evaluating Safety and Tolerability of Sepofarsen in Children 8 Years of Age With LCA10 Caused by Mutations in the CEP290 Gene
Sponsor: ProQR Therapeutics
Organization: ProQR Therapeutics

Organization Data

Organization: ProQR Therapeutics
Class: INDUSTRY
Study ID: PQ-110-005
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor: ProQR Therapeutics
Lead Sponsor Class: INDUSTRY
Responsible Party: None
Responsible Party Title: None
Responsible Party Type: SPONSOR
Responsible Party Affiliation: None
Old Name: None
Old Organization: None

Collaborators