Ignite Creation Date:
2025-12-24 @ 5:14 PM
Ignite Modification Date:
2026-01-21 @ 9:31 AM
Study NCT ID:
NCT03822650
Status:
COMPLETED
Last Update Posted:
2024-06-27
First Post:
2019-01-27
Is Gene Therapy:
True
Has Adverse Events:
False
Brief Title:
A Natural History Study of Neuronal Ceroid Lipofuscinosis Type 5 (CLN5)