Viewing StudyNCT04049084



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Last Modification Date: 2024-10-26 @ 1:15 PM
Study NCT ID: NCT04049084
Status: ENROLLING_BY_INVITATION
Last Update Posted: 2023-05-06
First Post: 2019-08-06

Brief Title: An Observational LTFU Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for ADA-SCID
Sponsor: University of California Los Angeles
Organization: University of California Los Angeles

Organization Data

Organization: University of California Los Angeles
Class: OTHER
Study ID: OTL-101-6
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor: University of California Los Angeles
Lead Sponsor Class: OTHER
Responsible Party: Donald B Kohn MD
Responsible Party Title: Principal Investigator
Responsible Party Type: PRINCIPAL_INVESTIGATOR
Responsible Party Affiliation: University of California Los Angeles
Old Name: None
Old Organization: None

Collaborators

Name Class
Great Ormond Street Hospital for Children NHS Foundation Trust OTHER