Viewing StudyNCT03964792



Ignite Creation Date: 2024-05-06 @ 1:13 PM
Last Modification Date: 2024-10-26 @ 1:10 PM
Study NCT ID: NCT03964792
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2024-01-09
First Post: 2019-05-14

Brief Title: Safety and Efficacy of Gene Therapy of the Sickle Cell Disease by Transplantation of an Autologous CD34 Enriched Cell Fraction That Contains CD34 Cells Transduced ex Vivo With the GLOBE1 Lentiviral Vector Expressing the βAS3 Globin Gene in Patients With Sickle Cell Disease DREPAGLOBE
Sponsor: Assistance Publique - Hôpitaux de Paris
Organization: Assistance Publique - Hôpitaux de Paris

Organization Data

Organization: Assistance Publique - Hôpitaux de Paris
Class: OTHER
Study ID: P170006J
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor: Assistance Publique - Hôpitaux de Paris
Lead Sponsor Class: OTHER
Responsible Party: None
Responsible Party Title: None
Responsible Party Type: SPONSOR
Responsible Party Affiliation: None
Old Name: None
Old Organization: None

Collaborators