Viewing StudyNCT03837184



Ignite Creation Date: 2024-05-06 @ 12:45 PM
Last Modification Date: 2024-10-26 @ 1:03 PM
Study NCT ID: NCT03837184
Status: COMPLETED
Last Update Posted: 2022-11-22
First Post: 2019-02-08

Brief Title: Single-Dose Gene Replacement Therapy Using for Patients With Spinal Muscular Atrophy Type 1 With One or Two SMN2 Copies
Sponsor: Novartis Gene Therapies
Organization: Novartis

Organization Data

Organization: Novartis
Class: INDUSTRY
Study ID: AVXS-101-CL-306
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor: Novartis Gene Therapies
Lead Sponsor Class: INDUSTRY
Responsible Party: None
Responsible Party Title: None
Responsible Party Type: SPONSOR
Responsible Party Affiliation: None
Old Name: None
Old Organization: None

Collaborators

Name Class
PRA Health Sciences INDUSTRY