Viewing Study NCT04105166


Ignite Creation Date: 2025-12-24 @ 4:44 PM
Ignite Modification Date: 2026-02-25 @ 5:33 PM
Study NCT ID: NCT04105166
Status: COMPLETED
Last Update Posted: 2025-09-05
First Post: 2019-09-24
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Gene Therapy for Pyruvate Kinase Deficiency (PKD)
Sponsor: Rocket Pharmaceuticals Inc.
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: RP-L301-0119
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators