Viewing Study NCT02230566


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Study NCT ID: NCT02230566
Status: COMPLETED
Last Update Posted: 2020-07-30
First Post: 2014-08-22
Is Gene Therapy: True
Has Adverse Events: True

Brief Title: A Phase 3 Study of UX003 Recombinant Human Betaglucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With Mucopolysaccharidosis Type 7 (MPS 7)
Sponsor: Ultragenyx Pharmaceutical Inc
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: UX003-CL301
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators